RECRUITINGOBSERVATIONAL
Longitudinal Study of Neurodegenerative Disorders
About This Trial
The purpose of this study is to understand the course of rare genetic disorders that affect the brain. This data is being analyzed to gain a better understanding of the progression of the rare neurodegenerative disorders and the effects of interventions.
Who May Be Eligible (Plain English)
Who May Qualify:
- Any patient with a genetic neurodegenerative disorder
Who Should NOT Join This Trial:
- none
Always talk to your doctor about whether this trial is right for you.
Original Eligibility Criteria
View original clinical language
Inclusion Criteria:
* Any patient with a genetic neurodegenerative disorder
Exclusion Criteria:
* none
Treatments Being Tested
OTHER
Palliative Care
Collecting information about the natural progression of these diseases
BIOLOGICAL
Hematopoetic Stem Cell Transplantation
Following patients who have received HSCT as part of their clinical care.
Locations (1)
UPMC Children's Hospital of Pittsburgh
Pittsburgh, Pennsylvania, United States