MPS I Clinical Trials
2 recruiting trials for MPS I. Eligibility criteria explained in plain English.
2
Total Trials
2
Recruiting Now
0
Phase 3 Trials
2
Sponsors
Recruiting Trials
RECRUITINGPhase 1NCT04532047
PEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
For detailed information, please view our study website: https://pearltrial.ucsf.edu/ The investigators aims to determine the the maternal and fetal safety and feasibility of in...
Sponsor: University of California, San FranciscoEnrolling: 101 location
RECRUITINGNCT03333200
Longitudinal Study of Neurodegenerative Disorders
The purpose of this study is to understand the course of rare genetic disorders that affect the brain. This data is being analyzed to gain a better understanding of the...
Sponsor: University of PittsburghEnrolling: 15001 location