Alpha-Mannosidosis Clinical Trials
2 recruiting trials for Alpha-Mannosidosis. Eligibility criteria explained in plain English.
2
Total Trials
2
Recruiting Now
0
Phase 3 Trials
2
Sponsors
Recruiting Trials
RECRUITINGPhase 1NCT02254863
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
The primary objective of the study is to determine the safety and feasibility of intrathecal administration of DUOC-01 as an adjunctive therapy in patients with inborn errors of...
Sponsor: Joanne Kurtzberg, MDEnrolling: 401 location
RECRUITINGNCT03333200
Longitudinal Study of Neurodegenerative Disorders
The purpose of this study is to understand the course of rare genetic disorders that affect the brain. This data is being analyzed to gain a better understanding of the...
Sponsor: University of PittsburghEnrolling: 15001 location