Metachromatic Leukodystrophy Clinical Trials
2 recruiting trials for Metachromatic Leukodystrophy. Eligibility criteria explained in plain English.
2
Total Trials
2
Recruiting Now
0
Phase 3 Trials
2
Sponsors
Recruiting Trials
RECRUITINGNCT03047369
The Myelin Disorders Biorepository Project
The Myelin Disorders Biorepository Project (MDBP) seeks to collect and analyze clinical data and biological samples from leukodystrophy patients worldwide to support ongoing and...
Sponsor: Children's Hospital of PhiladelphiaEnrolling: 1200020 locations
RECRUITINGNCT04925349
Modeling Macrophages Activation Pattern in X-linked Adrenoleukodystrophy, Metachromatic Leukodystrophy and Adult Onset...
This study is a national, non-randomized, open-label, multi-site with minimal risk study in adult with adrenomyeloneuropathy (AMN), childhood and adult subjects with cerebral ALD...
Sponsor: Assistance Publique - Hôpitaux de ParisEnrolling: 1002 locations