RECRUITINGOBSERVATIONAL
CuidAME: Longitudinal Data Collection From Patients With Spinal Muscular Atrophy in Spain
About This Trial
The goal of this observational study is to set up a longitudinal data collection study to perform a long-term follow-up of SMA patients in a real-world setting, and to standardise and homogenize the data collection process for SMA patient's data. Treated and untreated patients will be followed based on the routine clinical practice schedule.
Who May Be Eligible (Plain English)
Who May Qualify:
- Genetically confirmed 5q SMA
- Patient or caregivers written willing to sign a consent form has been obtained (except for paediatric patients deceased).
Who Should NOT Join This Trial:
- Further types of SMA (non-5q SMA).
- Patient without legal capacity who cannot understand the nature, significance, and consequences of the project.
Always talk to your doctor about whether this trial is right for you.
Original Eligibility Criteria
View original clinical language
Inclusion Criteria:
* Genetically confirmed 5q SMA
* Patient or caregivers written informed consent has been obtained (except for paediatric patients deceased).
Exclusion Criteria:
* Further types of SMA (non-5q SMA).
* Patient without legal capacity who cannot understand the nature, significance, and consequences of the project.
Locations (1)
Hospital Sant Joan de Déu
Esplugues de Llobregat, Spain