RECRUITINGOBSERVATIONAL
A Long-term Follow-up Study of Gaucher Disease
About This Trial
The study aims are to: a) identify the long-term natural history of Gaucher disease, b) evaluate long-term treatment efficacy of enzyme replacement therapy (ERT) and substrate reduction therapy (SRT), and c) identify potential long-term complications of this disorder. These aims will be accomplished through long-term record review of individuals with all three types of Gaucher disease.
Who May Be Eligible (Plain English)
Who May Qualify:
- Diagnosis of Gaucher Disease
Who Should NOT Join This Trial:
- Not meeting Inclusion criteria
Always talk to your doctor about whether this trial is right for you.
Original Eligibility Criteria
View original clinical language
Inclusion Criteria:
* Diagnosis of Gaucher Disease
Exclusion Criteria:
* Not meeting Inclusion criteria
Locations (1)
Duke University Medical Center
Durham, North Carolina, United States