Mucopolysaccharidosis VII Clinical Trials
2 recruiting trials for Mucopolysaccharidosis VII. Eligibility criteria explained in plain English.
2
Total Trials
2
Recruiting Now
0
Phase 3 Trials
2
Sponsors
Recruiting Trials
RECRUITINGNCT03604835
Mucopolysaccharidosis VII Disease Monitoring Program
The objectives of this study are to characterize MPS VII disease presentation and progression and assess long-term effectiveness and safety, including hypersensitivity reactions...
Sponsor: Ultragenyx Pharmaceutical IncEnrolling: 5014 locations
RECRUITINGNCT05619900
Registry of Patients Diagnosed With Lysosomal Storage Diseases
This is an international prospective and retrospective registry of patients with Lysosomal Storage Diseases (LSDs) to understand the natural history of the disease and the...
Sponsor: University of California, San FranciscoEnrolling: 2501 location