Mucopolysaccharidosis II Clinical Trials
2 recruiting trials for Mucopolysaccharidosis II. Eligibility criteria explained in plain English.
2
Total Trials
2
Recruiting Now
0
Phase 3 Trials
2
Sponsors
Recruiting Trials
RECRUITINGPhase 1NCT02254863
UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
The primary objective of the study is to determine the safety and feasibility of intrathecal administration of DUOC-01 as an adjunctive therapy in patients with inborn errors of...
Sponsor: Joanne Kurtzberg, MDEnrolling: 401 location
RECRUITINGNCT05619900
Registry of Patients Diagnosed With Lysosomal Storage Diseases
This is an international prospective and retrospective registry of patients with Lysosomal Storage Diseases (LSDs) to understand the natural history of the disease and the...
Sponsor: University of California, San FranciscoEnrolling: 2501 location