Homozygous Familial Hypercholesterolemia Clinical Trials
2 recruiting trials for Homozygous Familial Hypercholesterolemia. Eligibility criteria explained in plain English.
2
Total Trials
2
Recruiting Now
0
Phase 3 Trials
2
Sponsors
Recruiting Trials
RECRUITINGEarly Phase 1NCT06125847
NGGT006 Gene Therapy for Homozygous Familial Hypercholesterolemia
This is an early phase 1, open-label, single-center, dose-escalation, pilot trial to evaluate the safety and efficacy of an intravenous infusion of NGGT006 in homozygous familial...
Sponsor: First Affiliated Hospital Xi'an Jiaotong UniversityEnrolling: 121 location
RECRUITINGNCT04815005
HoFH, the International Clinical Collaborators Registry
Homozygous familial hypercholesterolemia (HoFH), a rare inherited disorder caused by bi-allelic mutations in the LDL Receptor pathway, is characterized by extremely elevated...
Sponsor: University of PennsylvaniaEnrolling: 10004 locations