Glycogen Storage Disease Type II Clinical Trials
2 recruiting trials for Glycogen Storage Disease Type II. Eligibility criteria explained in plain English.
2
Total Trials
2
Recruiting Now
0
Phase 3 Trials
1
Sponsors
Recruiting Trials
RECRUITINGPhase 4NCT06666413
China Post-approval Commitment (PAC) Study of Avalglucosidase Alfa in Participants With IOPD
This is a single group, 52-week treatment, Phase 4, open-label, single-arm study to assess the safety and efficacy of avalglucosidase alfa IV infusion in male and female Chinese...
Sponsor: Genzyme, a Sanofi CompanyEnrolling: 131 location
RECRUITINGNCT00231400
Pompe Disease Registry Protocol
The Pompe Registry is a global, multicenter, international, longitudinal, observational, and voluntary program for patients with Pompe disease, designed to track the disease's...
Sponsor: Genzyme, a Sanofi CompanyEnrolling: 200020 locations