Gaucher Disease Type 1 Clinical Trials
2 recruiting trials for Gaucher Disease Type 1. Eligibility criteria explained in plain English.
2
Total Trials
2
Recruiting Now
0
Phase 3 Trials
2
Sponsors
Recruiting Trials
RECRUITINGPhase 1 / Phase 2NCT06818838
A Clinical Study Evaluating LY-M001 Injection in the Treatment of Adult Patients With Type I Gaucher Disease
Gaucher disease (GD) is caused by mutations in the GBA1 gene, which leads to a lack or reduction of GCase activity. The consequences of this deficiency are generally attributed to...
Sponsor: Lingyi Biotech Co., Ltd.Enrolling: 123 locations
RECRUITINGPhase 1 / Phase 2NCT05487599
A Clinical Trial of PR001 (LY3884961) in Patients With Peripheral Manifestations of Gaucher Disease (PROCEED)
Study J3Z-MC-OJAE is a Phase 1/2, multicenter, open-label, dose-finding study of LY3884961 evaluating the safety and tolerability in adults with peripheral manifestations of GD....
Sponsor: Prevail TherapeuticsEnrolling: 158 locations